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Assessment of rAAVrh.74.MHCK7.micro-dystrophin Gene Therapy Using Magnetic Resonance Imaging in Children with Duchenne Muscular Dystrophy

  • Rebecca J. Willcocks
  • , Sean C. Forbes
  • , Glenn A. Walter
  • , Lee Sweeney
  • , Louise R. Rodino-Klapac
  • , Jerry R. Mendell
  • , Krista Vandenborne

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)E2031851
JournalJAMA Network Open
Volume4
Issue number1
DOIs
StatePublished - Jan 4 2021

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